Collaborators: Advocacy Groups Collaborators: Advocacy Groups USAExpandSMA Foundation Cure SMA FightSMA Gwendolyn Strong Foundation Miracle for Madison and Friends Muscular Dystrophy Association (MDA) SMA Angels Charity EuropeExpandEURORDIS SMA Europe TREAT-NMD ArgentinaExpandFamilias AME Argentina BrazilExpandAmigos Da Atrofia Muscular Espinhal CanadaExpandFamilies of SMA Czech RepublicExpandKolpingova rodina Smečno FranceExpandAssociation Française contre les Myopathies (AFM) GermanyExpandDeutsche Muskelstiftung (German Muscle Foundation) Initiative – Forschung und Therapie fuer SMA Deutsche Gesellschaft fuer Muskelkranke (DGM) Hong KongExpandFamilies of SMA Charitable Trust IsraelExpandFamilies of SMA ItalyExpandAssociazione per lo Studio delle Atrofie Muscolari Spinali Infantili (ASAMSI) The research against SMA Unione Italiana lotta alla Distrofia Muscolare Famiglie SMA New ZealandExpandFamilies of SMA RomaniaExpandAsociatia Werdnig Hoffman (AWH) SpainExpandFundación Atrofia Muscular Espinal SwitzerlandExpandSMA Schweiz TurkeyExpandSMA Grubu UkrainianExpandОрганизация Дети СМА (Children with SMA) United KingdomExpandSMA Support UK (previously The Jennifer Trust) The SMA Trust VenezulaExpandFamilias y Amigos de la Atrofia Muscular Espinal