Joint Program in Spinal Muscular Atrophy Enters First Stage of Clinical Development

South Plainfield, NJ, January 22, 2014 – PTC Therapeutics, Inc. (NASDAQ: PTCT), the SMA Foundation, and Roche (SIX: RO, ROG; OTCQX: RHHBY), announced today that their joint research program in Spinal Muscular Atrophy (SMA) has entered the first stage of clinical development aiming to assess safety and tolerability of an oral compound in healthy volunteers.…

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United States Senate Unanimously Passes the National Pediatric Research Network Act (NPRNA) Supporting SMA Research

United States Senate Unanimously Passes the National Pediatric Research Network Act (NPRNA) Supporting SMA Research Headed to the President’s desk today for signature, the legislation establishes a network of research consortia to focus on pediatric rare diseases, specifically including SMA.   Friday, November 15, 2013   Unanimously passed by the U.S. Senate on Thursday night,…

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Isis Reports Follow-Up Data From ISIS-SMN Rx Phase 1 Study In Children With Spinal Muscular Atrophy

Isis Reports Follow-Up Data From ISIS-SMN Rx Phase 1 Study In Children With Spinal Muscular Atrophy Improvements in muscle function continue to be observed up to fourteen months after a single dose CARLSBAD, Calif., Sept. 19, 2013 /PRNewswire/ — Isis Pharmaceuticals, Inc.(NASDAQ: ISIS) announced today that follow-up preliminary data from a single dose, open-label Phase…

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