Overview

Through the concerted efforts of drug companies, government agencies, academic institutions, and advocacy groups, the SMA community has reached an exciting point where new therapeutics have entered clinical trials or are approaching trials in the near future. Please visit the SMA Therapeutic Pipeline to learn more about various drug programs and their current stage of development based on publicly disclosed information.

The process of developing a new drug from the laboratory to the clinic can take over a decade and requires significant resources. Towards that goal of developing an effective therapeutic, the SMA Foundation has invested more than $60M in drug development programs and essential drug discovery assets.