Reports & Publications

The SMA Foundation team has created several reports and presentations on our own internal research and topics of interest for the SMA scientific community.

• Skeletal Muscle: a Critical Target in Treating SMA
• SMA Foundation Mouse Drug Testing Pipeline
  5 pages, 197 KB [PDF]
• SMA Foundation Allelic Series Mouse Models
  4 pages, 401 KB [PDF]
• Tools and Resources for the SMA biomarkers
  2 pages, 205 KB [PDF]
• Details on SMA Foundation's Biomarker Panel Developed with Rules-Based Medicine
  9 pages, 501 KB [PDF]
• SMN ELISA Validation and Use in Human and Mouse Samples
  1 page, 181 KB [PDF]
• Development of a Multiplex Immunoassay Biomarker Panel for SMA
  1 page, 691 KB [PDF]